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职业迁徙
个人简介
He has been culturing stem cells since 1992 and created the first mouse model for a recessive form of retinitis pigmentosa (RP) by applying genome engineering to stem cell technology in 1995. He successfully treated preclinical models of Pde6a, Pde6b, Mfrp, Rho, Cngb1 and autosomal recessive bestrophin retinopathies.
He has expertise in designing and testing genome engineering strategies in pre-clinical models, developing patient-specific knock-in models, generating of patient cell lines and providing care to patients with a precision medicine approach. He is also leading efforts in FDA trials for gene therapies, including PDE6A, RAB geranylgeranyl transferase, RPGR, CNGB3, CNGA3 and ABCA4 retinopathies.
He has expertise in designing and testing genome engineering strategies in pre-clinical models, developing patient-specific knock-in models, generating of patient cell lines and providing care to patients with a precision medicine approach. He is also leading efforts in FDA trials for gene therapies, including PDE6A, RAB geranylgeranyl transferase, RPGR, CNGB3, CNGA3 and ABCA4 retinopathies.
研究兴趣
论文共 687 篇作者统计合作学者相似作者
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AMERICAN JOURNAL OF OPHTHALMOLOGY (2024): 119-129
Cell reports medicineno. 4 (2024): 101459-101459
CELL AND BIOSCIENCEno. 1 (2024)
Advances in experimental medicine and biology (2023): 571-576
Advances in Experimental Medicine and Biology (2023): 103-107
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCEno. 8 (2023)
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Retinal cases & brief reports (2023)
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作者统计
#Papers: 686
#Citation: 18569
H-Index: 60
G-Index: 109
Sociability: 7
Diversity: 3
Activity: 216
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