Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis: A Randomized Clinical Trial.
Sabrina Paganoni,Christina N Fournier,Eric A Macklin, Lori B Chibnik,Melanie Quintana,Benjamin R Saville,Michelle A Detry,Matteo Vestrucci,Joe Marion,Anna McGlothlin,Senda Ajroud-Driss,Marianne Chase,Lindsay Pothier, Brittney A Harkey, Hong Yu,Alexander V Sherman,Jeremy M Shefner,Meghan Hall,Gale Kittle, James D Berry,Suma Babu,Jinsy Andrews,Derek Dagostino,Eric Tustison, Elisa Giacomelli, Erica Scirocco, Gustavo Alameda,Eduardo Locatelli,Doreen Ho,Adam Quick,Jonathan Katz,Daragh Heitzman, Stanley H Appel, Sheetal Shroff,Kevin Felice,Nicholas J Maragakis,Zachary Simmons,Timothy M Miller,Nicholas Olney,Michael D Weiss,Stephen A Goutman, Joseph Americo Fernandes,Omar Jawdat,Margaret Ayo Owegi, Laura A Foster,Tuan Vu,Hristelina Ilieva,Daniel S Newman,Ximena Arcila-Londono,Carlayne E Jackson,Shafeeq Ladha,Terry Heiman-Patterson,James B Caress,Andrea Swenson,Amanda Peltier,Richard Lewis,Dominic Fee, Matthew Elliott,Richard Bedlack,Edward J Kasarskis,Lauren Elman,Jeffrey Rosenfeld,David Walk,Courtney McIlduff,Paul Twydell,Eufrosina Young, Kristin Johnson,Kourosh Rezania,Namita A Goyal,Jeffrey A Cohen,Michael Benatar, Vovanti Jones,Jonathan Glass, Jaimin Shah,Said R Beydoun,James P Wymer, Lindsay Zilliox,Shakti Nayar,Gary L Pattee, Jennifer Martinez-Thompson,Brittany Harvey, Shital Patel, Paul Mahoney,Petra W Duda, Merit E Cudkowicz, HEALEY ALS Platform Trial Study Group JAMA network open(2025)
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