Targeted Allele-Specific FGFR2 Knockdown Via Human Recombinant Ferritin Nanoparticles for Personalized Treatment of Crouzon Syndrome
MOLECULAR THERAPY NUCLEIC ACIDS(2025)
关键词
MT: Oligonucleotides: Therapies and Applications,craniosynostosis,Crouzon syndrome,small interfering RNA,ferritin nanoparticles,gene silencing
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