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LBP-008 AAV8 Gene Therapy for Mitochondrial Neurogastrointestinal Encephalomyopathy

Teresa Brevini,Lisa Swift, Helen Reynolds, Richard Stopforth, Yogeshkumar Malam, John M. Ong,Harry VM Spiers, Emilija Jovanovic, Miki Scaravaglio, Vitushan Vakeeswarasarma,James A. Heslop, Sarah A. Hosgood,Claudia Fuchs,Michael Trauner, Adam Duckworth,Anna Paterson,Arthur Kaser,Jelle van den Ameele, Vasilis Kosmoliaptsis, Gwilym J. Webb,Christopher J. E. Watson,Andrew Butler,Fotios Sampaziotis

Journal of hepatology(2024)

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