ETV:SGSH, a Brain-Penetrant Enzyme Transport Vehicle for SGSH, Improves Lysosomal and Microglial Morphology, Degeneration and Cognitive Behavior in MPS IIIA MiceShababa T. Masoud,Hoang Nguyen,Claire Discenza,David Joy,Jeffrey Simms,Iris Lo, You Young Chun,Julia Holtzman, Khishig Tsogtbaatar,Amy Wing-Sze Leung,Isabel Becerra,Elliot Thomsen,Audrey Gill,Yashas Rajendra,Alexander Seay,Mohammad Jafarnejad,Anna Bakardjiev,Meredith E. K. Calvert,Cathal S. Mahon,Robert Thorne, Steven Chessler,Kirk Henne,Pascal Sanchez,Annie ArguelloMOLECULAR GENETICS AND METABOLISM(2024)引用 0|浏览13暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要