Dual-targeting CRISPR-CasRx reduces C9orf72 ALS/FTD sense and antisense repeat RNAs in vitro and in vivo
Liam Kempthorne,Deniz Vaizoglu, Alexander J. Cammack,Mireia Carcolé, Pacharaporn Suklai,Bhavana Muralidharan,François Kroll,Thomas G. Moens,Lidia Yshii,Stijn Verschoren, Benedikt V. Hölbling,Eszter Katona,Alla Mikheenko,Rachel Coneys,Paula de Oliveira,Yong-Jie Zhang, Karen Jansen,Lillian M Daughrity,Alexander McGown,Tennore M. Ramesh,Ludo Van Den Bosch,Ahad A. Rahim,Leonard Petrucelli,Jason Rihel,Adrian M. Isaacs biorxiv（2024）
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