OC 14.2 Pharmacokinetic Characteristics of ADAMTS13 in Patients with Congenital Thrombotic Thrombocytopenic Purpura: Interim Results from a Phase 3 Randomized, Controlled, Open-Label, Crossover Study

Research and Practice in Thrombosis and Haemostasis(2023)

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congenital thrombotic thrombocytopenic purpura,pharmacokinetic characteristics,adamts13,open-label
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