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Hematopoietic Cell Transplantation for Hematological Malignancies in Bloom Syndrome

Pediatric blood & cancer(2023)

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Pediatric Blood & CancerVolume 70, Issue 11 e30655 LETTER TO THE EDITOR Hematopoietic cell transplantation for hematological malignancies in Bloom syndrome Yohei Nishiyama, Yohei Nishiyama Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorKazuyoshi Mizuki, Kazuyoshi Mizuki Department of Pediatrics, St. Luke's International Hospital, Tokyo, JapanSearch for more papers by this authorAkihiro Hoshino, Akihiro Hoshino Department of Child Health and Development, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorShinsuke Hirabayashi, Shinsuke Hirabayashi Department of Pediatrics, Hokkaido University, Hokkaido, JapanSearch for more papers by this authorTatsuya Magara, Tatsuya Magara Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorMiho Ashiarai, Miho Ashiarai Department of Pediatrics, St. Luke's International Hospital, Tokyo, JapanSearch for more papers by this authorSatoshi Miyamoto, Satoshi Miyamoto Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorRintaro Ono, Rintaro Ono orcid.org/0000-0001-8847-2528 Department of Pediatrics, St. Luke's International Hospital, Tokyo, JapanSearch for more papers by this authorShuhei Takahashi, Shuhei Takahashi Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorYosuke Hosoya, Yosuke Hosoya Department of Pediatrics, St. Luke's International Hospital, Tokyo, JapanSearch for more papers by this authorDaiki Niizato, Daiki Niizato Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorHiroki Yoshihara, Hiroki Yoshihara Department of Pediatrics, St. Luke's International Hospital, Tokyo, JapanSearch for more papers by this authorAkira Nishimura, Akira Nishimura Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorNoriko Mitsuiki, Noriko Mitsuiki Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorTakahiro Kamiya, Takahiro Kamiya Department of Clinical Research Center, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorKei Takasawa, Kei Takasawa Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorMichiko Kajiwara, Michiko Kajiwara Center for Blood Transfusion and Cell Therapy, Tokyo Medical and Dental University Hospital, Tokyo, JapanSearch for more papers by this authorHirokazu Kanegane, Hirokazu Kanegane Department of Child Health and Development, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorTomohiro Morio, Tomohiro Morio Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorAtsushi Manabe, Atsushi Manabe Department of Pediatrics, Hokkaido University, Hokkaido, JapanSearch for more papers by this authorTakeshi Isoda, Takeshi Isoda orcid.org/0000-0003-3349-3705 Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorDaisuke Hasegawa, Corresponding Author Daisuke Hasegawa [email protected] orcid.org/0000-0002-9446-9568 Department of Pediatrics, St. Luke's International Hospital, Tokyo, Japan Correspondence Masatoshi Takagi, Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), 1-5-45 Yushima, Bunkyo-ku, Tokyo 113–8519, Japan. Email: [email protected] Daisuke Hasegawa, Department of Pediatrics, St. Luke's International Hospital, 9-1 Akashicho, Chuo-ku, Tokyo 104-8560, Japan. Email: [email protected]Search for more papers by this authorMasatoshi Takagi, Corresponding Author Masatoshi Takagi [email protected] orcid.org/0000-0002-7580-9184 Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, Japan Correspondence Masatoshi Takagi, Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), 1-5-45 Yushima, Bunkyo-ku, Tokyo 113–8519, Japan. Email: [email protected] Daisuke Hasegawa, Department of Pediatrics, St. Luke's International Hospital, 9-1 Akashicho, Chuo-ku, Tokyo 104-8560, Japan. Email: [email protected]Search for more papers by this author Yohei Nishiyama, Yohei Nishiyama Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorKazuyoshi Mizuki, Kazuyoshi Mizuki Department of Pediatrics, St. Luke's International Hospital, Tokyo, JapanSearch for more papers by this authorAkihiro Hoshino, Akihiro Hoshino Department of Child Health and Development, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorShinsuke Hirabayashi, Shinsuke Hirabayashi Department of Pediatrics, Hokkaido University, Hokkaido, JapanSearch for more papers by this authorTatsuya Magara, Tatsuya Magara Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorMiho Ashiarai, Miho Ashiarai Department of Pediatrics, St. Luke's International Hospital, Tokyo, JapanSearch for more papers by this authorSatoshi Miyamoto, Satoshi Miyamoto Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorRintaro Ono, Rintaro Ono orcid.org/0000-0001-8847-2528 Department of Pediatrics, St. Luke's International Hospital, Tokyo, JapanSearch for more papers by this authorShuhei Takahashi, Shuhei Takahashi Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorYosuke Hosoya, Yosuke Hosoya Department of Pediatrics, St. Luke's International Hospital, Tokyo, JapanSearch for more papers by this authorDaiki Niizato, Daiki Niizato Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorHiroki Yoshihara, Hiroki Yoshihara Department of Pediatrics, St. Luke's International Hospital, Tokyo, JapanSearch for more papers by this authorAkira Nishimura, Akira Nishimura Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorNoriko Mitsuiki, Noriko Mitsuiki Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorTakahiro Kamiya, Takahiro Kamiya Department of Clinical Research Center, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorKei Takasawa, Kei Takasawa Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorMichiko Kajiwara, Michiko Kajiwara Center for Blood Transfusion and Cell Therapy, Tokyo Medical and Dental University Hospital, Tokyo, JapanSearch for more papers by this authorHirokazu Kanegane, Hirokazu Kanegane Department of Child Health and Development, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorTomohiro Morio, Tomohiro Morio Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorAtsushi Manabe, Atsushi Manabe Department of Pediatrics, Hokkaido University, Hokkaido, JapanSearch for more papers by this authorTakeshi Isoda, Takeshi Isoda orcid.org/0000-0003-3349-3705 Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, JapanSearch for more papers by this authorDaisuke Hasegawa, Corresponding Author Daisuke Hasegawa [email protected] orcid.org/0000-0002-9446-9568 Department of Pediatrics, St. Luke's International Hospital, Tokyo, Japan Correspondence Masatoshi Takagi, Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), 1-5-45 Yushima, Bunkyo-ku, Tokyo 113–8519, Japan. Email: [email protected] Daisuke Hasegawa, Department of Pediatrics, St. Luke's International Hospital, 9-1 Akashicho, Chuo-ku, Tokyo 104-8560, Japan. Email: [email protected]Search for more papers by this authorMasatoshi Takagi, Corresponding Author Masatoshi Takagi [email protected] orcid.org/0000-0002-7580-9184 Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), Tokyo, Japan Correspondence Masatoshi Takagi, Department of Pediatrics and Developmental Biology, Tokyo Medical and Dental University (TMDU), 1-5-45 Yushima, Bunkyo-ku, Tokyo 113–8519, Japan. Email: [email protected] Daisuke Hasegawa, Department of Pediatrics, St. Luke's International Hospital, 9-1 Akashicho, Chuo-ku, Tokyo 104-8560, Japan. Email: [email protected]Search for more papers by this author First published: 29 August 2023 https://doi.org/10.1002/pbc.30655 Yohei Nishiyama and Kazuyoshi Mizuki contributed equally to this work. Read the full textAboutPDF ToolsRequest permissionExport citationAdd to favoritesTrack citation ShareShare Give accessShare full text accessShare full-text accessPlease review our Terms and Conditions of Use and check box below to share full-text version of article.I have read and accept the Wiley Online Library Terms and Conditions of UseShareable LinkUse the link below to share a full-text version of this article with your friends and colleagues. Learn more.Copy URL Share a linkShare onEmailFacebookTwitterLinkedInRedditWechat No abstract is available for this article. Supporting Information Filename Description pbc30655-sup-0001-SuppMat.pdf282.1 KB Supporting Information Please note: The publisher is not responsible for the content or functionality of any supporting information supplied by the authors. Any queries (other than missing content) should be directed to the corresponding author for the article. REFERENCES 1Sugranes TA, Flanagan M, Thomas C, Chang VY, Walsh M, Cunniff C. Age of first cancer diagnosis and survival in Bloom syndrome. Genet Med. 2022; 24(7): 1476-1484. 2Ma B, Corry J, Rischin D, Leong T, Peters LJ. Combined modality treatment for locally advanced squamous-cell carcinoma of the oropharynx in a woman with Bloom's syndrome: a case report and review of the literature. Ann Oncol. 2001; 12(7): 1015-1017. 3Hook GJ, Kwok E, Heddle JA. Sensitivity of Bloom syndrome fibroblasts to mitomycin C. Mutat Res. 1984; 131(5-6): 223-230. 4Kurihara T, Inoue M, Tatsumi K. Hypersensitivity of Bloom's syndrome fibroblasts to N-ethyl-N-nitrosourea. Mutat Res. 1987; 184(2): 147-151. 5Beamish H, Kedar P, Kaneko H, et al. Functional link between BLM defective in Bloom's syndrome and the ataxia-telangiectasia-mutated protein, ATM. J Biol Chem. 2002; 277(34): 30515-30523. 6Flanagan M, Cunniff CM. Bloom syndrome. In: MP Adam, GM Mirzaa, RA Pagon, eds. GeneReviews [Internet]. University of Washington, Seattle; 1993. 7Oertel M, Berdel C, Held G, et al. The new German evidence-based guideline on diffuse large B-cell lymphoma—key aspects for radiation oncologists. Strahlenther Onkol. 2023; 199(2): 115-120. 8Nie D, Zhang J, Xiong M, et al. Complete remission of refractory juvenile acute myeloid leukaemia with RUNX1-PRDM16 in Bloom syndrome after haematopoietic stem cell transplantation. Br J Haematol. 2020; 190(3): e166-e169. 9Locatelli F, Zecca M, Pession A, et al. The outcome of children with Fanconi anemia given hematopoietic stem cell transplantation and the influence of fludarabine in the conditioning regimen: a report from the Italian pediatric group. Haematologica. 2007; 92(10): 1381-1388. 10Kato K, Yoshida N, Matsumoto K, Matsuyama T. Fludarabine, cytarabine, granulocyte colony-stimulating factor and melphalan (FALG with L-PAM) as a reduced toxicity conditioning regimen in children with acute leukemia. Pediatr Blood Cancer. 2014; 61(4): 712-716. Volume70, Issue11November 2023e30655 ReferencesRelatedInformation
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