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Antibody-Oligonucleotide Conjugates (AOCs) Demonstrate Potent and Durable Exon Skipping and Dystrophin Restoration in a Mouse Model of Duchenne Muscular Dystrophy (S23.003)

Usue Etxaniz, Matthew Diaz, Raghav Bhardwaj, Olecya Tyaglo, Kellie Lemoine,Maria Azzurra Missinato, Aaron Andreson,Philip Kovach,Isaac Marks,Tyler Albin, Michael Cochran, Hae Won Kwon, Verna Zhao,Husam Younis, Mike Flanagan,Arthur A. Levin, Georgios Karamanlidis

Neurology(2022)

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