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Vector Shedding in Patients with DMD Treated with Delandistrogene Moxeparvovec and Seroconversion from Shed Vector in Naive Mice

Elizabeth S. Smith,Jyoti Malhotra,Sarah Lewis, Xiaolan Zhang, Damon R. Asher,Shufang Wang,Lilly East,Rachael Potter,Louise Rodino-Klapac

MOLECULAR THERAPY(2023)

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