Collaboration Between Patient Advocacy and Industry to Create a Master Protocol to Investigate the Novel Therapy Acetyl-L-leucine for Three Ultra-Rare Neurodegenerative Diseases: Niemann-Pick Type C, the GM2 Gangliosides and Ataxia-Telangiectasia
Molecular Genetics and Metabolism（2023）
AI Read Science
Must-Reading Tree
Example
Generate MRT to find the research sequence of this paper
Chat Paper
Summary is being generated by the instructions you defined