Use of 2,6-Diaminopurine As a Potent Suppressor of UGA Premature Stop Codons in Cystic Fibrosis
Catherine Leroy,Sacha Spelier,Nadege Charlene Essonghe, Virginie Poix,Rebekah Kong,Patrick Gizzi, Claire Bourban,Severine Amand,Christine Bailly,Romain Guilbert, David Hannebique, Philippe Persoons, Gwenaelle Arhant,Anne Prevotat,Philippe Reix,Dominique Hubert,Michele Gerardin,Mathias Chamaillard,Natalia Prevarskaya,Sylvie Rebuffat,George Shapovalov,Jeffrey Beekman,Fabrice Lejeune Molecular Therapy（2023）
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cystic fibrosis,nonsense mutation,readthrough molecule,2,6-diaminopurine,mouse model
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