Preclinical Studies in Support of Phase I/II Clinical Trials to Treat GUCY2D-associated Leber Congenital Amaurosis
Molecular therapy Methods & clinical development（2023）
关键词
AAV,adeno-associated virus,GUCY2D,Leber congenital amaurosis,LCA,LCA1,retGC1,retinal guanylate cyclase,gene therapy,inherited retinal disease
AI 理解论文
溯源树
样例
生成溯源树，研究论文发展脉络
Chat Paper
正在生成论文摘要