Treatment of Glutaric Aciduria Type 1 (GA-1) by GCDH Gene Replacement Therapy via Intracerebroventricular AAV9 DeliveryLu Guo, Tingting Shen, Zhi Ling, Xi Zhu, Wenjing Luo,Yuhuan Li,Zhikun Li,Wei Li,Xiaoping Zhao,Shin-Shay TianMOLECULAR THERAPY(2022)引用 0|浏览19暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要