Characterization of a Novel AAV Gene Replacement Therapy, VY-NPC101, In Vitro and In Vivo for the Treatment of Niemann-Pick Disease Type C1Elisabeth R. Knoll,Jenna Tocci,Brian Ezell, Eric Liu,Ambreen Sayed-Zahid, Mingwei Li,Holger Patzke,Todd Carter,Kelly Bales, Jeffrey Brown, Heather YonutasMOLECULAR THERAPY（2022）引用 0|浏览13暂无评分AI 理解论文溯源树样例生成溯源树，研究论文发展脉络Chat Paper正在生成论文摘要
