AXO-AAV-GM2 Gene Therapy for Infantile- and Juvenile-onset GM2 Gangliosidosis: Preliminary Results from an Ongoing Phase 1/2 TrialFlorian Eichler,Terence Flotte,Haley Andonian,Oguz Cataltepe,Rebecca Artinian,Albert Misko,Benjamin Thorp,John Jameson,Michael Sheehan,Toby Vaughn,Donna Valencia,Erika De BoeverMOLECULAR THERAPY(2022)引用 0|浏览17暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要