Betibeglogene Autotemcel Gene Therapy for Non–β0/β0 Genotype β-Thalassemia
Franco Locatelli,Alexis A. Thompson,Janet L. Kwiatkowski,John B. Porter,Adrian J. Thrasher,Suradej Hongeng,Martin G. Sauer,Isabelle Thuret,Ashutosh Lal,Mattia Algeri,Jennifer Schneiderman,Timothy S. Olson,Ben Carpenter,Persis J. Amrolia,Usanarat Anurathapan,Axel Schambach,Christian Chabannon,Manfred Schmidt,Ivan Labik,Heidi Elliot,Ruiting Guo,Mohammed Asmal,Richard A. Colvin,Mark C. Walters New England Journal of Medicine(2022)
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