Efficient and Precise Processing of the Optimized Primary Artificial MicroRNA in a Huntingtin-Lowering Adeno-Associated Viral Gene Therapy in Vitro and in Mice and Nonhuman Primates.
Human gene therapy（2022）
Key words
RNAi,artificial microRNA,Huntington's disease,huntingtin lowering,in vivo
AI Read Science
Must-Reading Tree
Example
Generate MRT to find the research sequence of this paper
Chat Paper
Summary is being generated by the instructions you defined