Bicistronic Aav Gene Therapy For Tay-Sachs And Sandhoff Diseases
Toloo Taghian,Deborah Fernau,Kalajan L. Mercado,Lauren Ellis,Elise Diffie,Amanda Gross,Anne S. Maguire,Ana Rita Batista,Stephanie Bertrand,Monique Otero,Rachel Prestigiacomo,Rachael Gately,Jillian Gallagher,Hannah Lahey,Amanda Taylor,Jey Koehler,Douglas R. Martin,Miguel Sena-Esteves,Heather L. Gray-Edwards MOLECULAR THERAPY(2021)
AI 理解论文
溯源树
样例