基本信息
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Career Trajectory
Bio
Dr. Ragni has actively pursued, initiated, collaborated, and participated in clinical translational research in congenital hemostasis and thrombosis disorders, serving as chair of clinical trials, prospective epidemiologic, observational, case-control studies, cost-effectiveness analyses, and investigator-initiated new drug trials in hemophilia and VWD. Her research studies were among the first multi-center NIH-funded investigator-initiated studies in hemophilia malignancy (NCI), hemophilia inhibitor formation (NHLBI), hemophilia HIV/HCV infection (NHLBI), hemophilia AIDS therapy (NIAID), and hemophilia adult prophylaxis (NHLBI). She co-chaired the NHLBI State of the Science (SOS) Inhibitor Prevention Trial Working Group (2018), and serves as PI of the Inhibitor Prevention and Eradication Platform Trial (HRSA). She also co-chaired the NHLBI SOS Hemophilia & VWD Subcommittee to design future trials, with three U34 trials funded NHLBI, and the VWDMin NHLBI U01 clinical trial to reduce bleeding in women with VWD, and the VWD-Woman trial prevent VWD postpartum bleeding (Takeda). She has collaborated on multi-center organ transplant HIV trials (NIAID), hemophilia gene therapy trials (NHLBI); VWD genotype-phenotype studies (NHLBI); novel therapeutics (fitusiran (siRNA AT) and hemlibra (emcizumab) and extended half-life protein trials (VIIa, VIII, IX) for hemophilia, and rhIL-11 and recombinant VWF for VWD. She has 9 active NIH grants, two of which she serves as PI; and local PI on 6 ATHN CDC grants.
Research Interests
Papers共 426 篇Author StatisticsCo-AuthorSimilar Experts
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Margaret V. Ragni, Jessica Callis,Nabil Daoud,Brian Hu,Matthew Manuel, Jarren Santos,Jonathan Schwartz, Kenneth D. Friedman,Peter Kouides,Philip Kuriakose,Andrew D. Leavitt,Ming Y. Lim,Nicoletta Machin,Michael Recht,Tammuella Chrisentery-Singleton
Pooja Vir,Devi Gunasekera,Batsukh Dorjbal,Dennis McDaniel, Atul Agrawal,Elizabeth P. Merricks,Margaret V. Ragni,Cindy A. Leissinger, Allen I. Stering,Kenneth Lieuw,Timothy C. Nichols,Kathleen P. Pratt
Journal of Thrombosis and Haemostasis (2024)
Blood Advances (2024)
Doris Quon,Shannon Jackson, María Teresa Alvarez-Román, Umer Khan, Sandra Casiano,Margaret V. Ragni, Savita Rangarajan
Blood advancesno. 18 (2024): 4751-4755
Blood Advances (2024)
Bloodno. Supplement 1 (2023): 5351-5351
Margaret V Ragni,Guy Young,Glaivy Batsuli, Emily Bisson,Shannon L Carpenter,Stacy E Croteau,Adam Cuker,Randall G Curtis,Michael Denne,Bruce Ewenstein, Amber Federizo,Neil Frick, Kerry Funkhouser,Lindsey A George,W Keith Hoots,Shawn M Jobe,Emily Krava,Christopher James Langmead,Roger J Lewis,José López,Lynn Malec,Ziva Mann,Moses E Miles,Emma Neely,Ellis J Neufeld,Glenn F Pierce,Steven W Pipe, Lisa R Pitler,Leslie Raffini,Kathaleen M Schnur,Jordan A Shavit
Expert review of hematologyno. sup1 (2023): 107-127
The Lancet. Haematologyno. 11 (2023): E870-E871
JOURNAL OF THROMBOSIS AND HAEMOSTASISno. 11 (2023): 3033-3044
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Author Statistics
#Papers: 425
#Citation: 16070
H-Index: 57
G-Index: 122
Sociability: 8
Diversity: 0
Activity: 3
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