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My laboratory develops new treatments for neurodegenerative diseases such as Huntington’s disease. We do this by first developing transgenic mouse models of specific human diseases, and then by testing new disease treatments in these mouse models. The YAC128 mouse model of Huntington’s disease accurately replicates the changes seen in humans with this disease, and is a critical tool that permits my laboratory to evaluate new treatment strategies in mice prior to undertaking large-scale clinical trials in human patients. Currently, my work is primarily focused on transgenic mouse models of Huntington’s disease, but in the future will expand to utilize the same standardized approach to investigate new therapeutics in mouse models of other devastating neurodegenerative disorders, such as ALS, prion disease, Parkinson's, and Alzheimer's disease.
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论文共 354 篇作者统计合作学者相似作者
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Marian DiFiglia,Blair R Leavitt,Douglas Macdonald, Leslie M Thompson, Huntington’s Disease Nomenclature Working Group:
Journal of Huntington's diseaseno. 2 (2024): 119-131
Nicholas S. Caron,Amirah E.-E. Aly,Hailey Findlay Black,Dale D.O. Martin,Mandi E. Schmidt,Seunghyun Ko,Christine Anderson,Emily M. Harvey,Lorenzo L. Casal,Lisa M. Anderson, Seyed M.R. Rahavi,Gregor S.D. Reid,Michael N. Oda,Danica Stanimirovic,Abedelnasser Abulrob,Jodi L. McBride,Blair R. Leavitt,Michael R. Hayden
Journal of Controlled Release (2024): 27-44
JOURNAL OF HUNTINGTONS DISEASEno. 1 (2024): 91-101
crossref(2024)
Ophthalmology and Therapyno. 4 (2023): 2049-2068
Fabricio Pio,Blair R. Leavitt
Contemporary clinical neurosciencepp.19-44, (2023)
Current research in neurobiology (2023): 100094-100094
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#Papers: 352
#Citation: 28746
H-Index: 83
G-Index: 168
Sociability: 8
Diversity: 0
Activity: 2
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