Intravenous delivery of AAV9-GLB1 gene therapy for GM1 gangliosidosis: An interim analysis Precilla D'Souza,Jean M. Johnston,Audrey Thurm,Cristan Farmer, Amanda L. Gross,Maria T. Acosta, Cynthia TifftMOLECULAR GENETICS AND METABOLISM(2024)引用 0|浏览0暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要