133 Long-term safety and efficacy of elexacaftor-tezacaftor-ivacaftor in children aged 6 and older with cystic fibrosis and at least one F508del allele: 144-week results of an open-label extension study

C. Wainwright,S. McColley, P. McNally, M. Powers,F. Ratjen,J. Rayment, G. Retsch-Bogart, E. Roesch,N. Ahluwalia, C. Chu, P. Menon, T. Weinstock,J. Davies

Journal of Cystic Fibrosis(2023)

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cystic fibrosis,long-term,elexacaftor-tezacaftor-ivacaftor,open-label
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