PB0355 Knock-in of Homozygous NBEAL2 Variants to Model Gray Platelet Syndrome in Megakaryocytes Derived from CRISPR-Cas9-edited Pluripotent Stem Cells

J. Collins,H. Foster,L. Mayer,A. Crosby,A. Evans, W. Lau, S. Mason, R. McDonald, T. Vallance,A. Waller,W. Ouwehand,E. Turro,C. Ghevaert, J. Guerrero

Research and Practice in Thrombosis and Haemostasis(2023)

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homozygous nbeal2 variants,model gray platelet syndrome,megakaryocytes,pluripotent stem cells,stem cells,crispr-cas
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