PB0355 Knock-in of Homozygous NBEAL2 Variants to Model Gray Platelet Syndrome in Megakaryocytes Derived from CRISPR-Cas9-edited Pluripotent Stem Cells
Research and Practice in Thrombosis and Haemostasis(2023)
关键词
homozygous nbeal2 variants,model gray platelet syndrome,megakaryocytes,pluripotent stem cells,stem cells,crispr-cas
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