Substantial Increases in Paroxysmal Nocturnal Hemoglobinuria (PNH) Red Blood Cell Clone Size With Oral Iptacopan Monotherapy Confirms Control of Hemolysis in Complement Inhibitor-Naive PNH Patients

CLINICAL LYMPHOMA MYELOMA & LEUKEMIA(2023)

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关键词
MDS, paroxysmal nocturnal hemoglobinuria, iptacopan, complement inhibitor, hemolysis, Phase III
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