Dose dependent lowering of alpha-synuclein and rescue of motor phenotype by miRNA-based AAV gene therapy
S. A. Broekmans,C. V. Tornero,F. Akyol,L. Toonen,S. Kieper,K. E. Ronde,W. Hogewerf,E. D. Tolsma,R. I. Seinstra,L. L. S. Janssen,E. A. A. Nolen,A. Valles