Maintenance therapy simplification using a single daily dose: A preliminary real-life feasibility study in patients with Wilson disease
Clinics and Research in Hepatology and Gastroenterology(2022)
摘要
•Wilson disease is treatable with multiple daily doses and lifelong treatment.•Multiple daily doses can be an obstacle for adherence and treatment efficacy.•In our study, a single daily dose is effective in most of stabilized WD patients.•SDD could represent a very interesting option to consider in some WD patients.•Our results encourage to set up a validation in a prospective study.
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关键词
Wilson disease,Wilson's disease,Single daily dose,Adherence,Compliance,Persistence,Long-term care
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