Maintenance therapy simplification using a single daily dose: A preliminary real-life feasibility study in patients with Wilson disease

Clinics and Research in Hepatology and Gastroenterology(2022)

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摘要
•Wilson disease is treatable with multiple daily doses and lifelong treatment.•Multiple daily doses can be an obstacle for adherence and treatment efficacy.•In our study, a single daily dose is effective in most of stabilized WD patients.•SDD could represent a very interesting option to consider in some WD patients.•Our results encourage to set up a validation in a prospective study.
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关键词
Wilson disease,Wilson's disease,Single daily dose,Adherence,Compliance,Persistence,Long-term care
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