Bicistronic AAV gene therapy for Tay-Sachs and Sandhoff diseases in a sheep modelT. Taghian,D. Fernau,K. Mercado,L. Ellis,E. Diffie,A. Gross, A. Maguire,A. Batista,S. Bertrand,M. Otero,R. Prestigiacomo,R. Gately,J. Gallagher, H. Lahey,A. Taylor,J. Koehler,D. Martin,M. Sena-Esteves,H. Gray-EdwardsMOLECULAR THERAPY(2021)引用 0|浏览5暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要