The avalglucosidase alfa phase 3 COMET trial in late-onset Pompe disease patients: Efficacy and safety results after 97 weeks
Priya Kishnani,Jordi Diaz-Manera,Hani Kushlaf,Shafeeq Ladha,Tahseen Mozaffar,Volker Straub,Antonio Toscano,Ans T. van der Ploeg,Kenneth I. Berger,Paula R. Clemens,Yin-Hsiu Chien,John W. Day,Sergey Illarioshkin,Mark Roberts,Shahram Attarian,Gerson Carvalho,Young-Chul Choi,Sevim Erdem-Ozdamar,Ozlem Goker-Alpan,Anna Kostera-Pruszczyk,Kristina An Haack,Nathan Thibault,Tianyue Zhou,Mazen M. Dimachkie,Benedikt Schoser MOLECULAR GENETICS AND METABOLISM（2022）
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avalglucosidase alfa,comet trial,disease patients,late-onset
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