The Force (Tm) Platform Achieves Robust Knock Down Of Toxic Human Nuclear Dmpk Rna And Foci Reduction In Dm1 Cells And In Newly Developed Htfr1/Dmsxl Mouse Model

Stefano Zanotti, Cody Desjardins,Nelson Hsia,Timothy Weeden, Ryan J. Russo,Lydia Schlaefke,Monica Yao,Aiyun Wen, Scott Hildebrand,John Najim,Qifeng Qiu, Brendan Quinn,Kim Tang,Mo Qatanani,Romesh Subramanian, Oxana Beskrovnaya

MOLECULAR THERAPY(2021)

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