Preliminary Outcomes of Haematopoietic Stem Cell Gene Therapy in a Patient with Mucopolysaccharidosis IIIAJane Kinsella,Karen Buckland,Heather Church, Beatriz Duran-Jimenez,Helena Lee,Stuart Ellison,Fred Vaz,Frits Wijburg,Farzin Farzaneh,Simon Jones,Adrian Thrasher,Rob Wynn,Brian W. BiggerMOLECULAR THERAPY(2020)引用 6|浏览2暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要